Atom | Ultra-Rare Gene-based Therapy (URGenT) Network Resource Access (X01, Clinical Trial Not Allowed)

Due Dates: May 31, 2025 | September 30, 2025 | January 31, 2026 | March 12, 2026

Funding Amounts: No direct funds awarded; provides in-kind access to contract research/medical organizations (CROs/CMOs) and subject matter experts for up to 2 years.

Summary: Provides investigators access to specialized resources and expertise within the NINDS URGenT Network to support planning, manufacturing, and limited nonclinical development of gene-based therapies for ultra-rare neurological or neuromuscular diseases.

Key Information: No funds awarded—support is in the form of resource access; clinical trials are not allowed under this mechanism.

Ultra-Rare Gene-based Therapy (URGenT) Network Resource Access (X01, Clinical Trial Not Allowed)

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