This grant funds innovative natural history studies to improve understanding and support medical product development for rare diseases with unmet needs.
Funds clinical trials testing new or existing treatments to improve care and expand approved uses for rare diseases with unmet medical needs.
Funding available for preclinical studies in rare diseases to show effectiveness of proposed treatments for potential further development into clinical trials.
This grant funds early phase clinical trials testing natural products like botanicals, probiotics, and dietary supplements with strong scientific backing for further testing.
This grant will fund research to improve clinical trial readiness for rare diseases by developing tools like biomarkers and outcome measures to help move new treatments or diagnostics toward successful trials.