Funding available for preclinical studies in rare diseases to show effectiveness of proposed treatments for potential further development into clinical trials.
NIH plans a milestone-driven award supporting planning and early to definitive clinical trials across biomedical and other interventions for up to 7 years; applications are not yet being accepted.
Funds clinical trials testing new or existing treatments to improve care and expand approved uses for rare diseases with unmet medical needs.
This grant funds innovative natural history studies to improve understanding and support medical product development for rare diseases with unmet needs.
This grant funds innovative natural history studies to advance medical product development and address unmet needs in rare diseases by generating high-quality, interpretable data.