Funding available for pilot projects researching rare diseases linked to understudied proteins, focusing on generating preliminary data and tools.
Funding available for preclinical studies in rare diseases to show effectiveness of proposed treatments for potential further development into clinical trials.
NIH supports clinical projects that prepare rare disease therapies or diagnostics for trials through biomarkers, outcome measures, or disease characterization; clinical trials are not allowed.
This grant funds clinical trials to test the safety and effectiveness of treatments for rare diseases, aiming to address unmet needs and support new or updated drug approvals.
This grant funds innovative natural history studies to improve understanding and support medical product development for rare diseases with unmet needs.
This grant funds innovative natural history studies to advance medical product development and address unmet needs in rare diseases by generating high-quality, interpretable data.